Cellectis

Case Summary

Gene therapy approach for sickle cell disease treatment

Source

Title

Pre-Clinical Development of a Highly Efficient TALEN ®-Based Correction of the β-Globin Gene in Patient-Derived Hematopoietic Stem and Progenitor Cells (HSPCs) to Treat Sickle Cell Disease

Type

academic paper

Year

2021

Confidence Score

90%