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Cellectis

🇫🇷 France·2021
Collected
Throughput AccountingBiotechnology

Case Summary

Gene therapy approach for sickle cell disease treatment

Source

Title
Pre-Clinical Development of a Highly Efficient TALEN ®-Based Correction of the β-Globin Gene in Patient-Derived Hematopoietic Stem and Progenitor Cells (HSPCs) to Treat Sickle Cell Disease
Type
academic paper
Year
2021
Confidence Score
90%
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